WP 3 : Development of new cellular models for drug screening
The objective of this WP is to:
- Develop an efficient drug screening assay using muscle cells from SMA patients and the most
performant cell culture system available to date for such purpose (CYTOO Myoscreen) - Use our unique know how to develop secondary and tertiary low throughput cell-based assays using
SMA muscle cells to respectively produce in vitro muscle fibers and muscle organoids.